Search Results
New ERT for Pompe Disease As Effective as Older ERT
ERT Home Infusions and Pompe Disease
How Duke University Has Led Pompe Disease Research
What's New in Pompe Disease
The Treatment of Pompe Disease: Clinical Updates in Newborn Screening and Enzyme Replacement
Gene Therapy and Pompe Disease: Preliminary Results From Phase I/II Study With AT845
Pompe Disease: Overview, Diagnosis Challenges, Treatments, and Emerging Therapies
VAL-1221 and Pompe Disease
The Pathophysiology of Pompe Disease
Best Practices and Future Considerations for Clinical Care of Pompe
John Crowley, Amicus Therapeutics discusses drug trial results for Pompe disease
Rare Disease Patients – Their Time Has Come
